Human Gene Therapy - April 2023 - 240

The Official Journal of the
European Society of Gene and Cell Therapy British Society for Gene and Cell Therapy French Society of Cell and Gene Therapy
Irish Society for Gene and Cell Therapy The Israeli Society of Gene & Cell Therapy German Society for Gene Therapy
Spanish Society of Gene and Cell Therapy Netherlands Society of Gene and Cell Therapy Finnish Society of Gene Therapy
Editor-in-Chief
Terence R. Flotte, MD
Celia and Isaac Haidak Professor ofMedical
Education
Dean of School ofMedicine
Provost and Executive Deputy Chancellor
University ofMassachusetts ChanMedical School
55 Lake Avenue North
Worcester, MA, USA 01655
Deputy Editor-in-Chief
Guangping Gao, PhD
Horae Gene Therapy Center & Department
of Microbiology and Physiology Systems
University ofMassachusetts ChanMedical School
368 Plantation Street, AS6-2049
Worcester, MA, USA 01605
European Editor
Hildegard Bu¨ning, PhD
Laboratory for Infection Biology
&Gene Transfer
Institute of Experimental Hematology
Hannover Medical School
OE 6960, J11
Carl-Neuberg-Str. 1
30625 Hannover
Germany
Asian Editor
Yu-Quan Wei, MD, PhD
National Key Laboratory of Biotherapy
and Cancer Center
West China Hospital, West China Medical
School, Sichuan University
Gaopeng Street, Keyuan Street Road 4, No. 1
Chengdu, Sichuan 610041
P.R. China
Executive Editor
Kevin Davies, PhD
Mary Ann Liebert, Inc., publishers
New Rochelle, NY, USA
Deputy Editors
Seng Cheng, PhD
Senior Vice President & ChiefScientific Officer,
Rare Disease
Pfizer
Andover, MA, USA
Mark A. Kay, MD, PhD
Departments of Pediatrics and Genetics
Stanford University School ofMedicine
Stanford, CA, USA
Thierry VandenDriessche, PhD
Department of Gene Therapy & Regenerative
Medicine
Vrije Universiteit Brussel
Brussels
Belgium
Department of Cardiovascular Sciences
Centerfor Molecular & Vascular Biology
University of Leuven
Leuven
Belgium
Associate Editors
Jennifer Adair, PhD
Stem Cell and Gene Therapy Program
Fred Hutchinson Cancer Research Center
Seattle, WA, USA
Robin R. Ali, PhD, FMedSci
Centre for Cell and Gene Therapy
King's College London
London, United Kingdom
Kellogg Eye Center
University of Michigan
Ann Arbor, MI, USA
K. Reed Clark, PhD
Ultragenyx Gene Therapy
Cambridge, MA, USA
Dongsheng Duan, PhD
Margaret Proctor Mulligan Professor
in Medical Research
University of Missouri
Columbia, MO, USA
Maria P. Limberis, PhD
Spirovant Sciences, Inc.
Philadelphia, PA, USA
Senior Consulting Editors
Jean Bennett, MD, PhD
Center for Advanced Retinal and Ocular
Therapeutics
Department of Ophthalmology
Perelman School ofMedicine
University of Pennsylvania
Philadelphia, PA, USA
J. Keith Joung, MD, PhD
Department of Pathology
Harvard Medical School
Boston, MA, USA
Molecular Pathology Unit
Massachusetts General Hospital
Charlestown, MA, USA
Center for Cancer Research and Center
for Computational and Integrative Biology
Massachusetts General Hospital
Charlestown, MA, USA
Carl H. June, MD
Department of Pathology and Laboratory
Medicine Center for Cellular
Immunotherapy
University of Pennsylvania
Perelman School ofMedicine
Philadelphia, PA, USA
Nathalie Cartier Lacave, MD
INSERM UMR1169: Biotherapy for
Neurodegenerative Diseases
CEA, Molecular Imaging Research Center
University Paris Saclay
Paris, France
Feng Zhang, PhD
Broad Institute ofMIT and Harvard
Cambridge, MA, USA
McGovern Institute for Brain Research
Massachusetts Institute of Technology
Cambridge, MA, USA
Howard Hughes Medical Institute
Cambridge, MA, USA
Scientific Editorial Board
Kari Airenne, PhD
Kuopio Center for Gene and Cell Therapy
Kuopio, Finland
Ramon Alemany, PhD
Institut Catala´ d'Oncologia-IDIBELL
Barcelona, Spain
Ian Edward Alexander, MD, PhD
Sydney Children's Hospitals Network
and Children's Medical Research
Institute
Sydney, Australia
Daniel G. Anderson, PhD
Massachusetts Institute of Technology
Cambridge, MA, USA
Aravind Asokan, PhD
Duke University
Durham, NC, USA
Takis Athanasopoulos, PhD
GlaxoSmithKline
Brentford, United Kingdom
Ana Rita Batista, PhD
University ofMassachusetts Chan
Medical School
Worcester, MA, USA
Christopher Baum, MD, PhD
Hannover Medical School
Hannover, Germany
Janet Benson, PhD, DABT
Lovelace Respiratory Research Institute
Albuquerque, NM, USA
Michael R. Betts, PhD
University of Pennsylvania Perelman
School ofMedicine
Philadelphia, PA, USA
Alessandra Biffi, MD
Harvard Medical School
Cambridge, MA, USA
Claire Booth, MBBS, PhD
Institute of Child Health
University College London
London, United Kingdom
Shannon E. Boye, PhD
University of Florida
Gainesville, FL, USA
Xandra O. Breakefield, PhD
Massachusetts General Hospital
Boston, MA, USA
Juan A. Bueren, PhD
CIEMAT
Madrid, Spain
David Bumcrot, PhD
Editas Medicine, Inc.
Cambridge, MA, USA
Barry J. Byrne, MD, PhD
University of Florida, College ofMedicine
Gainesville, FL, USA
Roberto Calcedo, PhD
Affinia Therapeutics
Waltham, MA, USA
Toni Cathomen, PhD
University of Freiburg
Freiburg im Breisgau, Germany
Joy A. Cavagnaro, PhD, DABT, ATS
Access BIO
Somerset, NJ, USA
Saswati Chatterjee, PhD
City of Hope National Medical Center
Duarte, CA, USA
Nathalie Cle´ment, PhD
Unicorn Consultations, LLC
Gainesville, FL, USA
Thomas J. Conlon, PhD
CR Scientific and Compliance Consulting,
LLC
Gainesville, FL, USA
Michelson FoundAnimals Foundation, LLC
Los Angeles, CA, USA
Kenneth Cornetta, MD
Indiana University School ofMedicine
Indianapolis, IN, USA
Larry A. Couture, PhD
Beckman Research Institute ofCity ofHope
Duarte, CA, USA
Gay M. Crooks, MB, BS
University of California-Los Angeles
Los Angeles, CA, USA
Pedro E. Cruz, PhD
ECBio, S.A.
Lisbon, Portugal
Ronald G. Crystal, MD
Weill Cornell Medical College
New York, NY, USA
Martin Donnelley, PhD
University ofAdelaide
Adelaide, South Australia
Boro Dropulic, PhD, MBA
Lentigen Corporation
Gaithersburg, MD, USA
Anja Ehrhardt, PhD
University ofMunich
Munich, Germany
John F. Engelhardt, PhD
University of Iowa
Iowa City, IA, USA
Erik Falck-Pedersen, PhD
Weill Cornell Medical College
New York, NY, USA
Boris Fehse, PhD
University Medical Center
Hamburg-Eppendorf
Hamburg, Germany
Keith Foster, PhD
University of Reading
Reading, England
Maria Cristina Galli, PhD
Istituto Superiore di Sanita`
Rome, Italy
Anne Galy, PhD
INSERM-Genethon
E´vry, France
Charles Gersbach, PhD
Duke University
Durham, NC, USA
Gloria Gonzalez-Aseguinolaza, PhD
Foundation for Applied Medical
Research (FIMA), University ofNavarra
Pamplona, Spain
Uta Griesenbach, PhD
Imperial College London
London, United Kingdom
Dirk Grimm, PhD
Heidelberg University
Heidelberg, Germany
Human Gene Therapy - April 2023

Table of Contents for the Digital Edition of Human Gene Therapy - April 2023
